{"id":49462,"date":"2018-09-25T01:00:00","date_gmt":"2018-09-26T01:58:40","guid":{"rendered":"http:\/\/www.05921.net\/index.php\/2018\/09\/26\/%e5%9f%ba%e5%9b%a0%e6%b2%bb%e7%96%97%e8%82%8c%e8%90%8e%e7%bc%a9-%e8%af%95%e9%aa%8c%e5%86%8d%e5%bc%80\/"},"modified":"2018-09-26T09:58:41","modified_gmt":"2018-09-26T01:58:41","slug":"%e5%9f%ba%e5%9b%a0%e6%b2%bb%e7%96%97%e8%82%8c%e8%90%8e%e7%bc%a9-%e8%af%95%e9%aa%8c%e5%86%8d%e5%bc%80","status":"publish","type":"post","link":"https:\/\/www.05921.net\/index.php\/49462\/","title":{"rendered":"\u57fa\u56e0\u6cbb\u7597\u808c\u840e\u7f29 \u8bd5\u9a8c\u518d\u5f00"},"content":{"rendered":"
\n

\u8fd9\u4e2a\u5728\u4f4d\u4e8e\u4fc4\u4ea5\u4fc4\u5dde\u7684\u54e5\u4f26\u5e03\u5168\u56fd\u513f\u7ae5\u533b\u9662\u8fdb\u884c\u7684\u4e34\u5e8a\u8bd5\u9a8c\uff0c\u521a\u521a\u6cbb\u7597\u7b2c\u4e09\u540d\u60a3\u8005\uff0c\u6548\u679c\u521d\u663e\u5c31\u88ab\u53eb\u505c\u3002<\/span><\/p>\n


<\/p>\n

7\u670825\u65e5\uff0c\u7f8e\u56fd\u98df\u54c1\u548c\u836f\u7269\u7ba1\u7406\u5c40\uff08FDA\uff09\u4e00\u7eb8\u901a\u77e5\uff0c\u8981\u6c42\u8bd5\u9a8c\u4e2d\u6b62\u3002\u6b64\u540e\uff0cSarepta\u516c\u53f8\u4e00\u76f4\u548cFDA\u6c9f\u901a\uff0c\u5e0c\u671b\u80fd\u591f\u7ee7\u7eed\u8bd5\u9a8c\u3002<\/span><\/p>\n


<\/p>\n

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<\/p>\n

\u8bd5\u9a8c\u53eb\u505c\u7684\u539f\u56e0\u662f\uff0c\u57fa\u56e0\u6cbb\u7597\u4e2d\u5b58\u5728\u4e0d\u7eaf\u7684\u7269\u8d28\u3002”\u7531\u4e8e\u7b2c\u4e09\u65b9\u63d0\u4f9b\u7684\u7814\u7a76\u7ea7\u8d28\u7c92\u4e2d\u5b58\u5728\u5fae\u91cf\u7684 DNA \u7247\u6bb5,” FDA \u53d1\u73b0\u3002<\/span><\/p>\n


<\/p>\n

\u4e3a\u6b64\uff0cSarepta \u5411 FDA\u6c9f\u901a\u5e76\u63d0\u4ea4\u4e86\u4e00\u4efd “\u884c\u52a8\u8ba1\u5212 “, \u5176\u4e2d\u5305\u62ec\u5bf9\u8d28\u7c92\u7684\u4f9b\u5e94\u5546\u8fdb\u884c\u5ba1\u8ba1\uff0c\u800c\u4e14\uff0c Sarepta \u627f\u8bfa\u4f7f\u7528\u7b26\u5408GMP \u6807\u51c6\u7684\u8d28\u7c92\u4f9b\u5e94\u5546\u3002<\/span><\/p>\n

\"\u57fa\u56e0\u6cbb\u7597\u808c\u840e\u7f29<\/p>\n


<\/span><\/p>\n

\u8fd9\u4e2a\u8bd5\u9a8c\u662f\u548c\u5168\u56fd\u513f\u7ae5\u533b\u9662(Nationwide Children\u2019s Hospital)\u7684\u6770\u745e-\u8499\u4ee3\u5c14\uff08Jerry Mendall\uff09\u533b\u751f\u5408\u4f5c\u8fdb\u884c\u7684\u3002<\/span><\/p>\n


<\/p>\n

\u4eca\u5e74\u5728\u676d\u5dde\u4e3e\u884c\u7684\u94b1\u6c5f\u9057\u4f20\u8bba\u575b\u4e0a\uff0c\u8499\u4ee3\u5c14\u533b\u751f\u8868\u793a\uff0c\u5f88\u5feb\u5c06\u5f00\u59cb\u8fdb\u884c\u7b2c\u4e00\u4f8b\u7684\u4eba\u4f53\u8bd5\u9a8c\u3002<\/span><\/p>\n


<\/p>\n

\u968f\u540e\uff0c\u5728\u513f\u7ae5\u533b\u9662\u5185\u8fdb\u884c\u7684\u4e34\u5e8a\u8bd5\u9a8c\uff0c\u4e09\u540dDMD\u7537\u5b69\u7387\u5148\u63a5\u53d7\u4e86\u8fd9\u4e2aMHCK micro-Dystrophin\u7684\u6cbb\u7597\u3002\u8bd5\u9a8c\u8ba1\u5212\u62db\u52df12\u540d\u60a3\u8005\u3002<\/span><\/p>\n


<\/span><\/p>\n

\u521d\u6b65\u7ed3\u679c\u663e\u793a\uff0c\u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u57fa\u56e0\u6cbb\u7597\u5bfc\u81f4\u5e73\u5747\u808c\u7ec6\u80de\u5b9a\u4f4d\u8f6c\u5bfc\u7684\u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u8868\u8fbe\u4e3a76.2\uff05\uff0c\u5e73\u5747\u7ea4\u7ef4\u5f3a\u5ea6\u4e3a74.5\uff05\u3002<\/span><\/p>\n


<\/p>\n

\u6cbb\u7597\u540e\u6d3b\u7ec4\u7ec7\u68c0\u67e5\u663e\u793a\uff0c\u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u6c34\u5e73\u7a33\u5b9a\uff0c\u5e73\u5747\u503c\u4e3a38.2\uff05\u3002<\/span><\/p>\n


<\/p>\n

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<\/p>\n

Sarepta\u9996\u5e2d\u6267\u884c\u5b98\u9053\u683c\u82f1\u683c\u62c9\u59c6\u8bf4, \u8be5\u516c\u53f8\u5e0c\u671b\u5728<\/span>\u4eca\u5e74\u5e74\u5e95\u4e4b\u524d\u5f00\u59cb\u8fdb\u884c\u57fa\u56e0\u6cbb\u7597\u8ba1\u5212\u7684\u6ce8\u518c\u8bd5\u9a8c<\/span>\u3002<\/span><\/p>\n


<\/p>\n

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<\/p>\n

“\u6211\u4eec\u6709\u4e00\u4e2a\u5f88\u5927\u7684\u91ce\u5fc3, \u5728\u4e24\u5e74\u5185\u53ef\u80fd\u5c06\u8fd9\u4e2a\u57fa\u56e0\u7597\u6cd5\u9020\u798f\uff08DMD\uff09\u793e\u533a, ” \u82f1\u683c\u62c9\u59c6\u5728\u63a5\u53d7 CNBC \u7684\u91c7\u8bbf\u4e2d\u8bf4\u3002<\/span><\/p>\n


<\/span><\/p>\n

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<\/span><\/p>\n


<\/span><\/p>\n

\"\u57fa\u56e0\u6cbb\u7597\u808c\u840e\u7f29<\/p>\n


<\/span><\/span><\/p>\n

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<\/span><\/p>\n

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<\/p>\n

Sarepta\u76ee\u524d\u5728\u7ade\u4e89\u4e2d\u6682\u65f6\u9886\u5148\uff0c\u4f46\u662f\uff0c\u516c\u53f8\u4e5f\u8868\u793a\uff0c\u591a\u803d\u8bef\u4e00\u5929\uff0c\u5c31\u6709\u53ef\u80fd\u5728\u8fd9\u573a\u7ade\u4e89\u4e2d\u5931\u53bb\u5934\u9a6c\u7684\u4f4d\u7f6e\u3002<\/span><\/p>\n


<\/p>\n

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<\/span><\/p>\n

\u53e6\u4e00\u65b9\u9762\uff0cSarepta\u6700\u8fd1\u597d\u4e8b\u591a\u78e8\u3002<\/span><\/p>\n


<\/p>\n

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<\/p>\n

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<\/p>\n

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\u8bf7\u7559\u8a00\u5206\u4eab\u770b\u6cd5\u3002<\/em><\/span><\/p>\n


<\/p>\n

\u4f60\u53ef\u80fd\u559c\u6b22<\/strong>\uff1a<\/span><\/p>\n

\u9047\u89c1\u57fa\u56e0\uff1a\u745e\u5e0c\u7684\u5c0f\u5e0c\u671b<\/span><\/a>
<\/p>\n

\u5b69\u5b50\u7b49\u4e0d\u53ca\uff01Sarapta\u5e74\u5185\u518d\u5f00\u57fa\u56e0\u8bd5\u9a8c\u9760\u8c31\u5417\uff1f<\/span><\/a>
<\/p>\n

DMD\u5468\u62a5\uff1a\u65b0\u836f\u4e2d\u56fd\u4e34\u5e8a\u8bd5\u9a8c \u5355\u6297\u57fa\u56e0\u6709\u559c\u6709\u5fe7<\/span><\/a>
<\/p>\n

\u5355\u6297\u62fc\u4e0d\u8fc7\u57fa\u56e0\uff1f\u8f89\u745e\u4e2d\u6b62\u7f55\u89c1\u75c5\u65b0\u836f\u4e34\u5e8a\u8bd5\u9a8c<\/span><\/a>
<\/p>\n


<\/p>\n

\u670d\u52a1\u65b0\u836f\u7814\u53d1 \u628a\u63e1\u6295\u8d44\u8d8b\u52bf<\/span><\/em><\/span><\/p>\n

\u6bcf\u5929\u7528\u65b0\u8bf4\u8bdd \u51b3\u7b56\u4e0d\u53ef\u6216\u7f3a<\/span><\/em><\/span><\/p>\n

\u5065\u70b9\u5b50ihealth<\/em><\/strong>\u662f\u533b\u836f\u884c\u4e1a\u9886\u5148\u7684\u6295\u8d44\u987e\u95ee\u8d44\u8baf\u5e73\u53f0\uff0c\u4e13\u6ce8<\/em>\u7f55\u89c1\u75c5\uff0c<\/strong>\u751f\u7269\u7c7b\u4f3c\u836f\uff0c<\/strong><\/em>\u65e5\u97e9\u5370\u5ea6<\/strong><\/em>\u5065\u5eb7\u884c\u4e1a\u7684\u6700\u65b0\u52a8\u5411\u3002<\/em><\/span><\/p>\n

\u4f60\u4e5f\u53ef\u4ee5\u5728\u4efb\u4f55\u5065\u70b9\u5b50\u6587\u7ae0\u540e\u7559\u8a00\u3002\u8bf7\u7b80\u77ed\u8bf4\u660e\u5177\u4f53\u9700\u6c42\u3002\u6211\u4eec\u4e00\u822c\u572824\u5c0f\u65f6\u4e4b\u5185\u8054\u7cfb\u3002<\/em><\/span><\/p>\n

<\/em><\/em><\/em><\/span><\/p>\n<\/p><\/div>\n","protected":false},"excerpt":{"rendered":"

\u8fd9\u4e2a\u5728\u4f4d\u4e8e\u4fc4\u4ea5\u4fc4\u5dde\u7684\u54e5\u4f26\u5e03\u5168\u56fd\u513f\u7ae5\u533b\u9662\u8fdb\u884c\u7684\u4e34\u5e8a\u8bd5\u9a8c\uff0c\u521a\u521a\u6cbb\u7597\u7b2c\u4e09\u540d\u60a3\u8005\uff0c\u6548\u679c\u521d\u663e\u5c31\u88ab\u53eb\u505c\u3002 7\u670825\u65e5\uff0c\u7f8e\u56fd […]<\/p>\n","protected":false},"author":1,"featured_media":49463,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":[],"categories":[2],"tags":[],"_links":{"self":[{"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/posts\/49462"}],"collection":[{"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/comments?post=49462"}],"version-history":[{"count":1,"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/posts\/49462\/revisions"}],"predecessor-version":[{"id":49466,"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/posts\/49462\/revisions\/49466"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/media\/49463"}],"wp:attachment":[{"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/media?parent=49462"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/categories?post=49462"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.05921.net\/index.php\/wp-json\/wp\/v2\/tags?post=49462"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}